New precision medicine ‘edits’ sickle cell gene and allows researchers to regrow normal blood cells.

Researchers at Johns Hopkins have successfully corrected a genetic error in stem cells from patients with sickle cell disease, and then used those cells to grow mature red blood cells, they report. The study represents an important step toward more effectively treating certain patients with sickle cell disease who need frequent blood transfusions and currently have few options.  The study is published in the journal … Continue reading New precision medicine ‘edits’ sickle cell gene and allows researchers to regrow normal blood cells.